Studies
Phase II open-label clinical trial evaluating efficacy of romiplostim added to standard of care for children and young adults with treatment naive and relapsed or refractory severe aplastic anemia
Pediatrics
Pediatric Subjects
Adult Subjects
A Phase 3, randomized, double-blind, placebo-controlled, multicenter study of mavorixafor in participants with congenital and acquired primary autoimmune and idiopathic chronic neutropenic disorders who are experiencing recurrent and/or serious infections
Pediatrics
Immunology
Autoimmune
Pediatric Subjects
Adult Subjects
The purpose of this study is to demonstrate the efficacy and evaluate the safety and tolerability of mavorixafor in participants with congenital or acquired primary autoimmune and idiopathic chronic neutropenic disorders who are experiencing recurrent and/or serious infections as assessed by demonstrating its clinical benefit and increasing levels of circulating neutrophils.
ATHN 10: Rare Coagulation Disorders
Pediatrics
Pediatric Subjects
Adult Subjects